ITVISMA is a prescription gene therapy used to treat adults and children 2 years of age and older with spinal muscular atrophy (SMA). ITVISMA is given as a one-time intrathecal injection. What is the ...
BridgeBio jumps on major clinical wins, strong launches and rare-disease programs targeting large markets with new drugs ...
Itvisma (onasemnogene abeparvovec-brve) demonstrated improved motor function and stabilization in patients regardless of SMA treatment history in Phase ...
US FDA approves Novartis’ Itvisma, the only gene replacement therapy for children two years and older, teens, and adults with SMA: Basel Wednesday, November 26, 2025, 09:00 Hrs ...
The performance of skilled behaviors requires a balance between consistency and adaptability. Although the neural mechanisms that regulate this balance have been extensively studied at systems and ...
I will now hand the conference call over to Vince Anzalone, Vice President of Investor Relations for Arrowhead. Please go ahead, Vince. Thank you, Andrew. Good afternoon, and thank you for joining us ...
Merck , known as MSD outside of the United States and Canada, today announced positive topline results from the Phase 2 CADENCE study evaluating WINREVAIRtm (sotatercept-csrk) in adults for the ...
Shanghai Henlius Biotech, Inc. (2696.HK), and Organon today announced that the US Food and Drug Administration (FDA) has approved the Biologics License Application (BLA) for POHERDY® (pertuzumab-dpzb) ...
Morning Overview on MSN
These seven Hemi engines were not built by Chrysler
The Hemi name is so tightly welded to Chrysler that it is easy to forget the combustion chamber shape itself is not ...
Merck plans a Phase 3 trial of Winrevair after a Phase 2 study testing it in CpcPH due to HFpEF hit its main goal.
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